PANTHERx Rare Chairman & CEO, Dr. Gordon Vanscoy, shares his experiences identifying opportunities, building businesses, and advancing the rare pharmacy industry on the podcast Going Deep with Aaron Watson. Listen to learn more about the origins of PANTHERx Rare, how we are helping foster solutions for people living with rare diseases, and the astounding rate […]

Read the Official PANTHERx Press Release. PANTHERx® Rare Pharmacy announces that it has been selected by Blueprint Medicines Corporation as a very limited distribution partner for breakthrough drug AYVAKIT™ (avapritinib). It has been approved for the treatment of adult patients with unresectable or metastatic gastrointestinal stromal tumor (GIST) harboring a PDGFRA exon 18 mutation, including […]

The end of the decade brought with it an exciting and critical trend for people living with rare diseases. Over the last eight years, the Center for Drug Evaluation and Research (CDER) approved more than twice as many orphan drugs as in the previous eight years (see graph below). It is often the case that […]

PANTHERx® Rare Pharmacy announces that it has been selected by Harmony Biosciences, LLC (Harmony) to distribute WAKIX® (pitolisant). PANTHERx is one of a select few specialty pharmacies providing nationwide access to the medication. “We are excited to be a part of the WAKIX® distribution network as we work with Harmony,” said Dr. Gordon Vanscoy, Chairman […]

Serving patients with rare, orphan, and devastating conditions is the reason PANTHERx Rare exists. The launch of our new website has created a platform through which we are able to relay our patients’ disease experiences. These stories are meant to illustrate the day to day struggles and the joys of being able to overcome some […]